Maroteaux-Lamy (MPS VI)
Synonyms: MPS VI
A Guide to Understanding Maroteaux-Lamy syndrome (Mucopolysaccharidosis (MPS) type VI) Source/Author: The MPS society Support group A booklet in pdf format on MPSVI, discussing the cause, inheritance, prenatal diagnosis, clinical problems (divided by body system), general treatment and management and specific treatment of MPSVI. Click on MPS VI to download booklet.
Cardiac Problems (in MPS disorders) Source/Author: The MPS society Support group Detailed overview of the cardiac problems in all of the mucopolysaccharidosis disorders. Click on article title to open pdf.
Enzyme replacement therapy for mucopolysaccharidosis VI: a phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-l Source/Author: Harmatz P, Giugliani R, Schwartz I, Guffon N, Teles EL, Miranda MC, Wraith JE, Beck M, Arash L, Scarpa M, Yu ZF, Wittes J, Berger KI, Newman MS, Lowe AM, Kakkis E, Swiedler SJ; MPS VI Phase 3 Study Group. Abstract Results on additional studies of enzyme replacement therapy in MPS VI.
Guia para entender el sindrome de Maroteaux-Lamy. Source/Author: The MPS society Support group IN SPANISH. A booklet in pdf format on MPSI, discussing the cause, inheritance, prenatal diagnosis, clinical problems (divided by body system), general treatment and management and specific treatment of MPSI. Click on MPSI to download booklet
Management Guidelines for Mucopolysaccharidosis VI Source/Author: Roberto Giugliani, MD, PhD, Paul Harmatz, MD and James E. Wraith, MD Medical Review Excellent overview of this condition, available treatments and discussion of how the various medical complications should be followed/addressed.
MPSVI.com Source/Author: BioMarin pharmaceuticals Web-based (medical) LINKS TO INFORMATION IN ENGLISH, PORTUGUESE, SPANISH, CHINESE, KOREAN, MALAY, TURKISH, JAPANESE AND TAIWAN. Overview of this condition and discussion of the enzyme replacement therapy that BioMarin has developed.
mucopolysaccharidosis (MPS) VI (Maroteaux-Lamy) Source/Author: Jablonski Syndromes Database Web-based (medical) Summary, clinical features, and medical bibliography.
MUCOPOLYSACCHARIDOSIS TYPE VI Source/Author: OMIM, Online Mendelian Inheritance in Man Medical/Scientific description of MPS VI with emphasis on the genetics of the condition.
Mucopolysaccharidosis type 6 Source/Author: R. Froissart and I. Maire; Orphanet Web-based (medical) IN FRENCH. Brief overview of the condition, scientific citations, clinical features and other web sites. Full text pdf available
ORTHOPEDIC DISORDERS IN CHILDREN WITH MPS/ML: A PARENTS' GUIDE Source/Author: Klane White, MD Support group Overview of orthopedic issues affecting patients with MPS disorders. Click on booklet title to download pdf.
Physical Therapy - For Professionals (for patients with MPS) Source/Author: The MPS society Support group How to provide PT for patients with MPS written by therapists experienced with these patients. Specifically written for physical therapists. Click on article title to download pdf.
PHYSICAL THERAPY FOR CHILDREN WITH MPS DISORDERS: INFORMATION FOR PARENTS Source/Author: Stacey C. Dusing, PT, MS, Angela Rosenberg, DrPH, PT, Sadye Paez, PT, MS Support group Information on the physical therapy needs of children with MPS disorders. Click on title to download pdf.
|